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CFUnite’s Virtual Presentation On Vertex Pharmaceuticals’ Orphan Drug Kalydeco (Ivacaftor)

January 17, 2013

CFUnite (Cystic Fibrosis Unite), had a virtual online event on Vertex Pharmaceuticals’ orphan drug Kalydeco (Ivacaftor) and the Cystic Fibrosis Transmembrane Regulator (CFTR) protein, on January 12, 2013.

CFUnite has 5 videos available on their website for those who weren’t able to participate in this event this past weekend. The videos are on the following topics :

–  Video #1 – Introduction to the event

–  Video #2 – Dr. David Sheppard, University of Bristol, discusses the Cystic Fibrosis Transmembrane Regulator (CFTR) protein that affects Cystic Fibrosis (CF)

–  Video #3 – Professor Stuart Elborn CBE, Queens University, Belfast, presents Phase III clinical trial results of Kalydeco for CF patients with G551D mutation

Video #4 – Dr. Michael Boyle, John Hopkins University, Baltimore USA, presents Phase II clinical trial results of Kalydeco + VX-809 given to CF patients with dF508

Video #5 –  Ed Owen, CEO of CF Trust UK – Discussion of what it is like for a patient to have CF and to take Kalydeco. Also, the “power of a united community of people with CF” is discussed.


Vertex Pharmaceuticals 4th Quarter 2012 & Year End Financial Results Conference Call – January 29, 2013, 5:00 PM ET.

Copyright © 2012-2013, Orphan Druganaut Blog. All rights reserved.

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