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What Are The Top Rare Disease Product Areas For 2012 ?

February 1, 2013

       In the February 2013 issue of Medical Marketing & Media, the publication looks at rare diseases, identifies some of the unique challenges that companies face in this space, and identifies the most concentrated orphan drug categories with fascinating statistics.

Interesting points made in the article :

–  Commercial blockbuster success of Alexion Pharmaceuticals hematology drug Soliris and Novartis cancer drug Gleevec due to “ … premium pricing and the ability to push into multiple indications (Reference Blog Post “Orphan Drug Company Life Cycle Management Strategy: Multiple Indications”)

–  Table titled, “Top Rare Disease Product Areas, 2012”, identifies the most concentrated orphan drug categories by their # of FDA-approved products + following statistics :

  1. Global Sales & % change over previous 12 months
  2. US total media spend & % change over previous 12 months
  3. US DTC (Direct-to-consumer) spend
  4. US journal spend dollars.

–   Companies active in the rare disease market tend to be small-to-medium size

–   Companies in the rare disease market are replacing the traditional blockbuster drug model with a new orphan drug model

–  For rare diseases, it is not the big Pharma’s blockbuster mass marketing, but a very “targeted form of communication” focused on the rare disease patient, treatment physician, and working closely with the rare disease advocacy organizations.

The most concentrated orphan drug categories identified are :

–         Hemophilia

–         Chronic Myelogenous Leukemia

–         Chronic Lymphocytic  Leukemia

–         Pulmonary Arterial Hypertension

–         Lennox-Gastaut Syndrome

–         Multiple Sclerosis

–         Angioedema/HAE

–         Cystic Fibrosis

–         Mucopolysaccaridosis.

Copyright © 2012-2013, Orphan Druganaut Blog. All rights reserved.

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